Gilead Sciences, Inc. (Nasdaq: GILD) announced that the Anti-Infective Drugs Advisory Committee of the U.S. Food and Drug Administration (FDA) has recommended that aztreonam for inhalation solution be approved for the treatment of infections due to Pseudomonas aeruginosa (P. aeruginosa) in patients with cystic fibrosis (CF). The committee voted 15 to 2 that Gilead has [...]

Protalix Biotherapeutics, Inc. (NYSE-Amex: PLX) announced the completion of its New Drug Application (NDA) submission with the U.S. Food and Drug Administration (FDA) for taliglucerase alfa, a plant-cell expressed form of glucocerebrosidase (GCD) for the potential treatment of Gaucher’s disease.

The Medical College of Georgia is leading an initiative that could result in a paradigm shift in the care of patients with sickle cell disease.
Morehouse University School of Medicine and University of Florida are partners in the initiative that is enlisting primary care physicians across Georgia to serve as “medical homes” for patients, changing how [...]

Born with a retinal disease that made him legally blind, and would eventually leave him totally sightless, the nine-year-old boy used to sit in the back of the classroom, relying on the large print on an electronic screen and assisted by teacher aides. Now, after a single injection of genes that produce light-sensitive pigments in [...]

IDBS, the leading worldwide provider of research data management and analytics solutions to R&D organizations, today announced that The Children’s Hospital of Philadelphia (CHOP), one of the leading pediatric hospitals and research facilities in the world, has implemented the InforSense-based Translational Research Solution to advance the understanding of complex genetic disease. Using the solution, CHOP [...]